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Treatable Diseases

Research on Stem cell therapy has shown that these could be used to treat more than 75 life-threatening diseases. Some of these include

Cancers: Many cancers including: Acute and Chronic Myelogenous Leukemia, Acute Lymphoblastic Leukemia Blood Disorders: Thalessemia, Sickle Cell Disease, Fanconi's Anemia

Immuno Deficiencies: Kostmann Syndrome, Omenn's Syndrome, Severe Combined Immunodeficiency (SCID) Familial Disorders: Breast Cancer Musculoskeletal Connective Tissue Disorders: Osteopetrosis Metabolic/Storage Disorders: Hunter's Disease, Leukodystophies

Check out the complete list of Treatable Diseases with Stem Cell Transplant

  • Acute Biphenotypic Leukemia
  • Acute Lymphoblastic Leukemia (ALL)
  • Acute Myelofibrosis
  • Acute Myelogenous Leukemia (AML)
  • Acute Undifferentiated Leukemia
  • Adrenoleukodystrophy
  • Advanced Chronic Lymphocytic Leukemia (CLL)
  • Agnogenic Myeloid Metaplasia(myelofibrosis)
  • Amegakaryocytosis / Congenital Thrombocytopenia
  • Amegakaryocytic thrombocytopenia
  • Aplastic Anemia (Severe)
  • Ataxia-Telangiectasia
  • Bare Lymphocyte Syndrome
  • Batten disease (inherited neuronal ceroid lipofuscinosis)
  • Beta Thalassemia Major
  • Blackfan-Diamond anemia
  • Breast Cancer
  • Burkitt's Lymphoma
  • Cartilage-Hair Hypoplasia
  • Chediak-Higashi Syndrome
  • Chronic Granulomatous Disease
  • Chronic Myelogenous Leukemia (CML)
  • Chronic Myelomonocytic Leukemia (CMML)
  • Common Variable Immunodeficiency
  • DiGeorge Syndrome
  • Dyskeratosis congenita
  • Essential Thrombocythemia
  • Evans syndrome
  • Ewing Sarcoma
  • Familial Erythrophagocytic Lymphohistiocytosis
  • Fanconi Anemia
  • Gaucher's Disease
  • Glanzmann Thrombasthenia
  • Gunther disease
  • Hemophagocytosis
  • Histiocytosis-X
  • Hodgkin's Disease
  • Hunter's Syndrome (MPS-II)
  • Hurler's Syndrome (MPS-IH)
  • Juvenile Chronic Myelogenous Leukemia (JCML)
  • Juvenile Myelomonocytic Leukemia (JMML)
  • Kostmann's Syndrome
  • Krabbe Disease
  • Langerthans cell histiocytosis
  • Lesch-Nyhan Syndrome
  • Leukocyte Adhesion Deficiency
  • Liposarcoma
  • Maroteaux-Lamy Syndrome (MPS-VI)
  • Metachromatic Leukodystrophy
  • Morquio Syndrome (MPS-IV)
  • Mucolipidosis II (I-cell Disease)
  • Multiple Myeloma
  • Myelofibrosis Myeloid Metaplasia
  • Myelodysplastic Syndrome
  • Chronic Myelomonocytic Leukemia
  • Refractory anemia with excess blasts in transformation
  • Neutrophil Actin deficiency
  • Neuroblastoma
  • Niemann-Pick Disease
  • Non-Hodgkin's Lymphoma
  • Omenn's Syndrome
  • Osteopetrosis
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)
  • Pancytopenia
  • Plasma Cell Leukemia
  • Polycythemia Vera
  • Prolymphocytic Leukemia
  • Pure Red Cell Aplasia
  • Refractory Anemia (RA)
  • Refractory Anemia wih Excess Blasts (RAEB/RAEB-T)
  • Refractory Anemia w/ Ringed Sideroblasts (RARS)
  • Renal Cell Carcinoma
  • Reticular Dysgenesis
  • Retinoblastoma
  • Sanfilippo Syndrome (MPS-III)
  • Scheie Syndrome (MPS-IS)
  • Severe Combined Immunodeficiency (SCID)
  • Sickle Cell Anemia
  • Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
  • Thalassemia (Cooley's anemia)
  • Thymic dysplasia
  • Waldenstrom's Macroglobulinemia
  • Wiskott-Aldrich syndrome
  • Wolman Disease
  • X-linked lymphoproliferative Disorder (XLP)
 


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